KMT2A/MLL Drug Discovery Landscape & Assay Solutions

Histone Methyltransferase Inhibitors & Menin-MLL Disruptors for MLL-Rearranged and NPM1-Mutant Acute Leukemias. High-purity recombinant SET domains, interaction partners, and lentiviral systems for next-generation epigenetic drug development.

TarMart Solution Ecosystem & Related Targets

Comprehensive reagent toolkit for KMT2A/MLL drug discovery. Select your modality below:

Component / Network Product Description Product Link
Enzyme Target KMT2A/MLL SET Domain Recombinant Protein
Active methyltransferase domain (residues 3765-3969), Sequence Verified, >95% purity, HEK293 expressed.
View KMT2A Products
PPI Partner MEN1 (Menin) Recombinant Protein
Full-length binding partner for MLL complex interaction assays, High Purity (>95%).
View MEN1 Products
Complex Component WDR5 Recombinant Protein
WD40 repeat protein, critical for MLL complex assembly, Endotoxin <1EU/µg.
View WDR5 Products
Gene Delivery KMT2A Lentivirus Premade Particles
Full-length ORF or SET domain for stable cell line construction in leukemia models.
View KMT2A Products
Benchmark Ab Anti-KMT2A/MLL Recombinant Antibody
Sequence-defined positive control for Western/IP, validated for ChIP compatibility.
View KMT2A Products
Validator KMT2A/MLL siRNA Set (3 unique sequences)
For specific knockdown verification in MLL-r leukemia cell lines.
View KMT2A Products
Related Target A MEN1 (Menin)
Direct binding partner; co-target for MLL-Menin disruption strategies.
View MEN1 Products
Related Target B WDR5
Core COMPASS subunit essential for KMT2A methyltransferase assembly.
View WDR5 Products
Related Target: DOT1L DOT1L Recombinant Protein
Downstream methyltransferase in MLL-rearranged leukemia; synergy target.
View DOT1L Products
Selectivity Panel KMT2B SET Domain Protein
Paralog for selectivity screening (avoid KMT2B toxicity), Sequence Verified.
View KMT2B Products
Critical Assay Challenge The TarMart Advantage (Technical Spec)
KMT2 Family Selectivity (KMT2B/C/D off-target) Homolog Panel Available: Human KMT2A, KMT2B, KMT2C, KMT2D SET domains with >95% purity, identical expression systems (HEK293) for consistent assay kinetics.
Menin-MLL PPI Disruption Validation Truncated MLL1 peptides (residues 2826-2930) and Full-length MEN1 protein for AlphaScreen/SPR assay development.
Cellular Context (Nuclear Entry) Lentivirus for Stable Cell Lines: KMT2A wild-type and MLL-AF9 fusion constructs in leukemia cell models; preserve native chromatin context.
Resistance Mutation Screening Menin Mutant Proteins (MEN1 V101G, F27A, A59T) and KMT2A interface variants for mechanistic resistance studies.
Drug Resistance Modeling Human/Mouse orthologs and site-directed mutant recombinant proteins available with >95% purity.
Lack of Assay Controls Clinical-grade benchmark antibodies and Menin protein pairings available.

Live KMT2A/MLL R&D Tracker

Market data changes daily. Access the latest global pipeline status directly:

Global Clinical Landscape & Future Outlook

The race for KMT2A/MLL-targeted therapeutics has shifted decisively toward Menin-MLL protein-protein interaction (PPI) disruption, with first-generation inhibitors (revumenib, ziftomenib) showing clinical efficacy in MLL-rearranged and NPM1-mutant acute leukemias. As these agents advance through Phase II/III, the next wave of R&D focuses on direct SET domain inhibitors (addressing resistance mutations at the Menin interface) and PROTAC degraders capable of eliminating both wild-type and fusion oncoproteins. Key players include Syndax (Revumenib, Phase III), Kura Oncology (Ziftomenib, Phase II), Johnson & Johnson (JNJ-75276617), Biomea Fusion (BMF-219), and Daiichi Sankyo (DS-1594). The field is increasingly differentiating between MLL-rearranged leukemia (dependent on Menin-MLL interaction) and solid tumor applications, where KMT2A wild-type function may require distinct inhibition strategies. Combination therapies with BCL-2 inhibitors (Venetoclax), FLT3 inhibitors, and DOT1L inhibitors are being actively explored to overcome resistance and improve durable responses.

Competitive Modality & Indication Snapshot

Modality Representative Players Key Indications Critical Assay Need (Why TarMart?)
Menin-MLL Inhibitor (Small Molecule) Syndax (Revumenib), Kura Oncology (Ziftomenib), J&J (JNJ-75276617), Biomea Fusion (BMF-219) MLL-r AML/ALL, NPM1-mutant AML PPI Disruption Assay: MEN1 + MLL1 peptide (2826-2930) with High Purity (>95%) for AlphaScreen/FP
Direct SET Domain Inhibitor Daiichi Sankyo (DS-1594), Discovery-stage programs Refractory AML, Solid Tumors Enzymatic Activity Assay: Full SET domain with proper cofactor (SAM) binding; Selectivity panel vs KMT2B required
PROTAC Degrader Preclinical (Universities, Biotech) MLL-r Leukemia, MDS Cell-Based Degradation: Lentivirus-expressed KMT2A-Fusion constructs for t1/2 measurements
Combination (Menin + DOT1L) Various Academia High-Risk MLL-r Dual Target Validation: KMT2A + DOT1L proteins for mechanistic synergy studies
WDR5-MLL Inhibitor Discovery Phase / Academia Solid Tumors, AML Selectivity Assay (Need structural homolog proteins)

Key Functional Domains & Mutations

Based on UniProt Q03164, KMT2A contains the following key domains: SET domain (catalytic), Bromo domain, FYR N-terminal, FYR C-terminal. Clinically relevant mutations include dbSNP:rs9332745, rs9332747, and rs9332772, which are documented in UniProt. These mutations may impact drug binding or protein stability and are critical for resistance modeling.


This integrated analysis combines knowledge from multiple intelligence streams to provide a comprehensive, non-redundant overview of the KMT2A/MLL landscape.